Browsing: drug

Ultomiris has become one of the most important treatments in the rare disease space because of its ability to reduce the burden of chronic infusion therapy while improving patient outcomes across paroxysmal nocturnal hemoglobinuria (PNH), atypical hemolytic uremic syndrome (aHUS), and generalized myasthenia gravis (gMG). As a long-acting C5 complement inhibitor, Ultomiris was developed as…

Researchers at King’s College London have identified a promising new strategy for tackling Alzheimer’s disease by targeting several of the disease’s earliest biological changes at the same time. Their study found that KCL-286, an experimental drug originally developed for spinal cord injury that has already passed Phase 1 safety trials, reduced multiple hallmarks of Alzheimer’s…